| Symbol | Name | Country | Exchange |
|---|---|---|---|
| CYTH | Cyclo Therapeutics, Inc. | US | NASDAQ |
| FOLD | Amicus Therapeutics, Inc. | US | NASDAQ |
| PASG | Passage Bio, Inc. | US | NASDAQ |
| SIOX | Sio Gene Therapies Inc. | US | NASDAQ |
| TSHA | Taysha Gene Therapies, Inc. | US | NASDAQ |
| OZYMF | Orphazyme A S | US | OTC |
| 086890 | ISU Abxis Co. Ltd | KR | KQ |
| LYS | Lysogene SA | FR | PA |
| PLX | Protalix Biotherapeutics Inc | IL | TA |
| BM8 | BioMarin Pharmaceutical Inc | DE | F |
| PBDA | PROTALIX BIOTHERAP.DL-01 | DE | F |
| RB0 | REGENXBIO Inc | DE | F |